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Ultragenyx Pharmaceutical Inc. NASDAQ Listed Jan 31, 2014
Healthcare ·Biotechnology ·US · ultragenyx.com
$26.14
After hrs $26.12 +0.00%
Mkt Cap $2.6B
52w Low $18.29 32.6% of range 52w High $42.37
50d MA $22.70 200d MA $27.70
P/E (TTM) -4.2x
EV/EBITDA -6.2x
P/B
Debt/Equity -15.9x
ROE 718.8%
P/FCF -4.8x
RSI (14)
ATR (14)
Beta 0.25
50d MA $22.70
200d MA $27.70
Avg Volume 2.1M
Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Europe, and internationally. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; Dojolvi for treating long-chain fatty acid oxidation disorders; and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia. The company's products candidatures include DTX401, an adeno-associated virus 8 (AAV8) gene therapy clinical candidate for the treatment of patients with glycogen storage disease type Ia; DTX301, an AAV8 gene therapy for the treatment of patients with ornithine transcarbamylase; UX143, a human monoclonal antibody for the treatment of osteogenesis imperfecta; GTX-102, an antisense oligonucleotide for the treatment of Angelman syndrome; UX701, for the treatment of Wilson disease; and UX053 for the treatment of glycogen storage disease type III. Ultragenyx Pharmaceutical Inc. has collaboration and license agreement with Kyowa Kirin Co., Ltd.; Saint Louis University; Baylor Research Institute; REGENXBIO Inc.; Bayer Healthcare LLC; GeneTx; Mereo; University of Pennsylvania; Arcturus Therapeutics Holdings Inc., Solid Biosciences Inc.; and Daiichi Sankyo Co., Ltd. Ultragenyx Pharmaceutical Inc. was incorporated in 2010 and is headquartered in Novato, California.
SIC Code
2834
CIK (SEC)
Phone
415 483 8800
60 Leveroni Court · Novato, CA 94949 · US
Data updated apr 26, 2026 9:54pm · Source: massive.com